Clinical Trials

    HELIOS-B: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy

    Investigator: Mahwash Kassi

    Study Coordinator: Jan-Michael Ragunton

    Status: Open Not Enrolling

    ClinicalTrials.gov Number: NCT04153149

    Phone: 346.238.0218

    Protocol Number: PRO00027010

    Description


    This study will evaluate the efficacy and safety of vutrisiran 25 mg administered subcutaneously (SC) once every 3 months (q3M) compared to placebo in patients with ATTR amyloidosis with cardiomyopathy.